An enrolling clinical trial is assessing whether a “booster shot” of a COVID-19 vaccine can improve the immune response in…
Articles by Marisa Wexler, MS
Eurordis opened a campaign, called Rare 2030 Action, that is seeking to establish a European action plan for…
Galapagos NV and Gilead Sciences are discontinuing all clinical trials with the investigational medication ziritaxestat. This includes the…
Small genetic variations that alter gene activity could play a role in the development of scleroderma and open new…
Scleroderma treatment TMB-003, which aims to improve patients’ quality of life by reducing the scarring that characterizes the…
A new documentary, “Beyond Breathless,” will showcase the journey of those affected by interstitial lung disease (ILD) through the…
The National Organization for Rare Disorders (NORD)’s RareLaunch training program will host two days of free virtual workshops…
A majority of rare disease patients using telehealth during the COVID-19 pandemic thought the experience positive, and many would like…
Autologous hematopoietic stem cell transplant (AHSCT) — replacing patients’ damaged bone marrow with their own healthy blood stem cells…
Talaris Therapeutics has raised $115 million in financing, which will be used to support the clinical…